Expanding rare disease drug trials based on shared molecular etiology.

Authors

Brooks, Pj; Tagle, Danilo; Groft, Steve;

Keywords

  • Clinical Trials as Topic/ methods
  • Drug Design
  • Humans
  • Molecular Targeted Therapy/ methods
  • Rare Diseases/ classification
  • Rare Diseases/ drug therapy
  • Rare Diseases/ metabolism

External Links